Achondroplasia Insights

FDA Approves New Treatments for Children

April 09, 2025 • Estimated Reading Time: 1 minute

Latest Research

A recent study focused on evaluating the content validity of clinical outcome assessments for children and adolescents with achondroplasia. This research emphasizes the need for reliable tools to assess their experiences, as well as those of their families. The study aims to ensure these assessments accurately reflect the needs of individuals with achondroplasia.

By involving both children and families, the study takes a comprehensive approach to understanding achondroplasia's impact across different age groups. This could lead to more personalized care strategies. Developing tailored assessments is crucial for capturing unique challenges and improving overall care and quality of life, as noted by (Hoover-Fong, 2025).

Clinical Trials

This is a list of upcoming or ongoing clinical trials that are actively recruiting and have been listed or updated in the last two weeks:

A Study of TYRA-300 in Children With Achondroplasia: BEACH301

View the full list of clinical trials →

Community News

Little People of AmericaApr 02, 2025

The past 24 hours have been amazing, exciting, and a whirlwind! While we had a bit of an overwhelming start, we appreciate your patience as conference registration opened. We love that there was so much enthusiasm that we broke the internet! (Okay, maybe just the registration site 😆)

We’re thrilled to share that over 1,400 people have already registered—that may be a record!

Reservations are fluctuating by the hour as we are trying to make room for everyone. We are in constant contact with the hotel and are working out rooms for everyone who is registered. If you are not registered and still reserved a room, don't be surprised if your room goes back to the regular Hyatt price (which is a lot more money than just registering for conference).

🎟️ Event tickets are updated by the minute. We are working on adding some additional tickets to the baseball game, city tour, and SEAL tour, just to name a few. If you missed tickets for something yesterday or today, keep checking back. We're doing our best to add more tickets when possible!

🚨 HOTEL UPDATE: The hotel is not sold out! If you’re unable to book certain dates, reserve what you can and email [email protected] with the dates you need added to your reservation.

Thank you for the love and support for our favorite event of the year! We can’t wait to see you all in San Diego! 😎

The MAGIC FoundationApr 02, 2025

It's go time!! Print this flyer and take it to your endocrinologists office. Ask them to put them up in their waiting room, exam rooms, hallways, etc. Wherever they can grab the attention of their patients, is where we want to be!!

The more people we can get to this year's convention, the more lifelong memories, connections, and friendships we can make.💓

Dwarf Athletic Association of AmericaApr 03, 2025

Now you get eight straight weeks of posts reminding you that there is no late or on-site registration! Register for the #DAAA2025 National Games at the link in our profile today! You have until May 31st!